We’re the leading resource for those affected by bleeding disorders. You can count on our organization to ensure your voice is heard. It’s with your help that we can make a difference. Learn more and get involved.
Nationally recognized researcher Dr. Leonard Valentino to lead the Foundation into the future.
Groups argue patients need a quick resolution to ensure access to care.
The group of patients who participated in this study were teenagers living with hemophilia A and B, who averaged 16 years of age.
The activity is intended for emergency medicine physicians, hematologists, pediatricians, nurses, and other healthcare professionals who manage patients with hemophilia.
On December 23rd, the BioMarin submitted a Biologics License Application for valoctocogene roxaparvovec to the U.S. Food and Drug Administration.